Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE)
… Mingozzi 01/03/2024 Molecular Metabolism The myotubular and centronuclear myopathy patient registry: a … 14/12/2023 Molecular Therapy - Methods and Clinical Development Safety and efficacy of gene replacement therapy … Stem Cell Research CRISPR-Cas9 KO Cell Line Generation and Development of a Cell-Based Potency Assay for rAAV-FKRP Gene …Article publié le: mer 20/09/2023 - 07:25