Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE)
… centronuclear myopathy patient registry: a multifunctional tool for translational research Anna Buj-Bello 01/02/2024 … citrullinemia type I mouse model by neonatal gene-targeting combined to SaCRISPR-Cas9 Fanny Collaud, Giuseppe Ronzitti … citrullinemia type I mouse model by neonatal gene-targeting combined to SaCRISPR-Cas9 Fanny Collaud, Giuseppe Ronzitti …Published on: