Approches génétiques intégrées et nouvelles thérapies pour les maladies rares (INTEGRARE)
… citrullinemia type I mouse model by neonatal gene-targeting combined to SaCRISPR-Cas9 Fanny Collaud, Giuseppe Ronzitti … gene therapy for rare pediatric diseases: Lessons learned from clinical experience with AAV vectors Antoine Gardin, … Generation of three induced pluripotent stem cell lines from patients with glycogen storage disease type III Lucille …Published on: Wed 20/09/2023 - 07:25